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CME

Gene Therapy for Monogenic Diseases

Monogenic diseases, of which there are thousands, are caused by a mutation in a single gene.
CME credit is no longer available for this conference.

Course Authors

Matthew H. Porteus, M.D., Ph.D.

Dr. Porteus is Assistant Professor of Pediatrics, Graduate School of Biomedical Sciences, University of Texas Southwestern Medical School, Dallas, Texas. Within the past 12 months, Dr. Porteus no commercial conflicts of interest.

Estimated course time: 1 hour(s).

Albert Einstein College of Medicine – Montefiore Medical Center designates this enduring material activity for a maximum of 1.0 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

In support of improving patient care, this activity has been planned and implemented by Albert Einstein College of Medicine-Montefiore Medical Center and InterMDnet. Albert Einstein College of Medicine – Montefiore Medical Center is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.

 
Learning Objectives

Upon completion of this Cyberounds®, you should be able to:

  • Describe the different types of viral vectors that are being used in gene therapy

  • Summarize the successes and setbacks in the recent clinical trials for gene therapy

  • Describe the future directions of gene therapy research to improve the safety of gene therapy.

 

TERMS AND CONDITIONS

This conference may include discussion of commercial products and services.

The opinions expressed herein are those of the authors and do not necessarily represent the views of the sponsor or its publisher. Please review complete prescribing information of specific drugs or combination of drugs, including indications, contraindications, warnings and adverse effects before administering pharmacologic therapy to patients.

 

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